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Disease models, In vitro pharmacology
Identification of 2,2-Dimethylbutanoic Acid (HST5040), a Clinical Development Candidate for the Treatment of Propionic Acidemia and Methylmalonic Acidemia
Armstrong AJ, Henke BR, Collado MS, et al. April 13, 2021
Doi: 10.1021/acs.jmedchem.1c00124